Improving access to our medicines is part of our commitment to patients – and fundamental to our responsibility as a company.
Rare diseases are often severe, life-threatening and complex conditions. Every day, we work tirelessly to champion for the estimated 350 million people living with rare diseases around the world.1 We are driven by our passion for pursuing breakthrough science where no therapy currently exists.
As a company, we have a fundamental responsibility to ensure that patients who need our medicines are able to access them. Our commitment to patients includes improving access to therapies regardless of where patients may live. Shire has delivered on this commitment by providing charitable donations of our products for patients with rare, genetic, hematologic, and immunologic conditions. And we continue to explore options for charitable donations through strong partnerships with third-party organizations that help identify the greatest areas of unmet patient needs around the world.
Our Charitable Access Program for Genetic Diseases
We have a unique responsibility to champion underserved patient communities, which is why we have partnered with several non-governmental organizations to provide our Charitable Access Program (CAP) to patients with rare and genetic diseases outside the United States.
Shire’s CAP is currently available for patients with three of the most common lysosomal storage disorders, including Fabry disease, Gaucher disease and Hunter syndrome.
Shire’s CAP provides contributions of medical products to nonprofits and non-governmental organizations in select countries where:
- Shire products are not available
- Some patients have been diagnosed
- No local regulatory filing is planned (or is more than 12-24 months away), and
- In-country capabilities exist to safely and effectively administer treatments.
This patient-centric program focuses on ensuring stable and continuous access to treatment for underserved patient communities and, at the same time, supporting country capability building for sustainable long-term patient care.
For more information about Shire’s Charitable Access Program, please contact email@example.com.
- Global Genes. Global Genes Factsheet on Rare Diseases. https://globalgenes.org/rare-diseases-facts-statistics/